Greig, J. A. et al. Nat. Biotechnol. https://doi.org/10.1038/s41587-023-01974-7 (2023).
Nathwani, A. C. et al. Blood 132 (Suppl. 1), 491 (2018).
Pasi, K. J. et al. N. Engl. J. Med. 382, 29–40 (2020).
Article CAS PubMed Google Scholar
George, L. A. et al. N. Engl. J. Med. 385, 1961–1973 (2021).
Article CAS PubMed PubMed Central Google Scholar
Muhuri, M., Levy, D. I., Schulz, M., McCarty, D. & Gao, G. Mol. Ther. 30, 1364–1380 (2022).
Article CAS PubMed PubMed Central Google Scholar
Nakai, H. et al. J. Virol. 75, 6969–6976 (2001).
Article CAS PubMed PubMed Central Google Scholar
Sun, X. et al. Hum. Gene Ther. 21, 750–761 (2010).
Article CAS PubMed PubMed Central Google Scholar
Fong, S. et al. Nat. Med. 28, 789–797 (2022).
Article CAS PubMed PubMed Central Google Scholar
Sabatino, D. E. et al. Mol. Ther. 30, 2646–2663 (2022).
Article CAS PubMed PubMed Central Google Scholar
Dalwadi, D. A. et al. Mol. Ther. 29, 2898–2909 (2021).
Comments (0)